paediatrics

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Touchdown for Rocket as its first gene therapy gets US okay

Rocket Pharma has won FDA approval for the first gene therapy for LAD-I, a devastating genetic disorder causing severe vulnerability to infections.

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Ascendis scores FDA approval for weekly dwarfism drug

Children with achondroplasia will soon have the option of a once-weekly - rather than daily - injection, courtesy of Ascendis' newly approved Yuviwel.

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UK will cover transport costs for children with cancer

Families of young people with cancer in England will have the costs of travelling to medical appointments covered under a new funding scheme.

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CDC cuts recommended childhood jabs from 17 to 11

The CDC has upended the childhood vaccination schedule, cutting the number of recommended shots in a move that has dismayed medical organisations.

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CDC panel votes to scrap hepatitis B birth dose advice

CDC advisers vote to overturn decades of US policy and abandon endorsement of universal hepatitis B vaccination for newborns in the US.

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Medical group advises against leucovorin for autism

The American Academy of Paediatrics has warned against leucovorin as a treatment for autism, citing a lack of evidence on safety and efficacy.

Touchdown for Rocket as its first gene therapy gets US okay

Ascendis scores FDA approval for weekly dwarfism drug

UK will cover transport costs for children with cancer

CDC cuts recommended childhood jabs from 17 to 11

CDC panel votes to scrap hepatitis B birth dose advice

Medical group advises against leucovorin for autism

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